Researchers identified a unique protein signature in the blood of BMD and LGMD patients that may reflect disease progression.

Summer can be rough for folks with muscular dystrophy, columnist Patrick Moeschen writes, but it can also bring adventures in appreciation.

Ifetroban improved heart function and reduced cardiac damage biomarkers in people with DMD in a Phase 2 clinical trial.

Columnist Betty Vertin is grateful to have the help of a hired caregiver, but it's also been a difficult adjustment, she says.

The FDA has granted rare pediatric disease designation to PBGENE-DMD, an experimental gene-editing therapy for Duchenne ...

A recent dream leaves columnist Robin Stemple questioning how his disability progression due to FSHD affects his family and ...

The U.S. Food and Drug Administration is due to review data on deramiocel, a cell therapy up for approval for heart disease ...

Caregiving means that columnist Betty Vertin sometimes misses out on activities with her children who don't have DMD. Finding balance is key.

A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.

Duvyzat’s approvals were based on the Phase 3 EPIDYS trial (NCT02851797), which included 179 boys, ages 6 and older, who were able to walk. The boys received Duzyvat or a placebo twice a day for 18 ...

I feel equally blessed to be celebrating 45 years with Wendy. She knew about my facioscapulohumeral muscular dystrophy (FSHD) before we got married. She knew that at some point, hopefully far down the ...

Gene therapy designed for muscle cells SRP-9003 is designed to deliver a healthy copy of the SGCB gene to muscle cells, to enable beta-sarcoglycan protein production. In order to deliver its genetic ...