Researchers identified a unique protein signature in the blood of BMD and LGMD patients that may reflect disease progression.

Ifetroban improved heart function and reduced cardiac damage biomarkers in people with DMD in a Phase 2 clinical trial.

Summer can be rough for folks with muscular dystrophy, columnist Patrick Moeschen writes, but it can also bring adventures in appreciation.

The FDA has granted rare pediatric disease designation to PBGENE-DMD, an experimental gene-editing therapy for Duchenne ...

The U.S. Food and Drug Administration is due to review data on deramiocel, a cell therapy up for approval for heart disease ...

A recent dream leaves columnist Robin Stemple questioning how his disability progression due to FSHD affects his family and ...

A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.

Approved exon-skipping therapies Exondys 51 Exondys 51 (eteplirsen) was developed by Sarepta Therapeutics as a treatment for DMD patients with mutations amenable to exon 51 skipping. That’s about 13% ...

No description.Betty Vertin is a mother and writer living in rural Hastings, Nebraska, with her husband and seven children. Betty is a caregiver to three sons, Max, Rowen, and Charlie. Her oldest was ...

Heart problems in different disease types Duchenne muscular dystrophy Virtually all people with Duchenne muscular dystrophy (DMD) will develop some degree of cardiomyopathy by the time they reach ...

Doctors can use several tests to diagnose muscular dystrophy (MD). A correct diagnosis gives patients an understanding of how their disease is likely to progress. It also helps doctors do a better job ...

Becker muscular dystrophy is a condition in which skeletal and heart muscles slowly degrade. The causes and symptoms of Becker are similar to those of Duchenne muscular dystrophy, though the disease’s ...